Sickle Cell Disease - Pipeline Review, H2 2016 - Global Markets Direct - Market Research

Sickle Cell Disease - Pipeline Review, H2 2016

Sickle Cell Disease - Pipeline Review, H2 2016 - Global Markets Direct - Market Research
Sickle Cell Disease - Pipeline Review, H2 2016
Published Oct 29, 2016
199 pages — Published Oct 29, 2016
Price US$ 2,000.00  |  Buy this Report Now

About This Report

  
Abstract:

Summary

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Sickle Cell Disease Pipeline Review, H2 2016, provides an overview of the Sickle Cell Disease (Hematological Disorders) pipeline landscape.

Sickle cell anemia is a genetic (inherited) blood disorder in which red blood cells, which carry oxygen around the body, develop abnormally. Signs and symptoms include anemia, delayed growth, vision problems, pain and frequent infections. Treatment includes antibiotics, pain relievers, blood transfusion and stem cell transplant.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Sickle Cell Disease Pipeline Review, H2 2016, provides comprehensive information on the therapeutics under development for Sickle Cell Disease (Hematological Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Sickle Cell Disease (Hematological Disorders) pipeline guide also reviews of key players involved in therapeutic development for Sickle Cell Disease and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 1, 2, 8, 9, 1, 24, 7 and 2 respectively for Similarly, the Universities portfolio in Phase II, Phase I, Preclinical and Discovery stages comprises 1, 1, 5 and 1 molecules, respectively for Sickle Cell Disease.

Sickle Cell Disease (Hematological Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Directs proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

- The pipeline guide provides a snapshot of the global therapeutic landscape of Sickle Cell Disease (Hematological Disorders).
- The pipeline guide reviews pipeline therapeutics for Sickle Cell Disease (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Sickle Cell Disease (Hematological Disorders) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Sickle Cell Disease (Hematological Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
- The pipeline guide encapsulates all the dormant

  
Source:
Document ID
GMDHC8604IDB
Industry
Format:
PDF Adobe Acrobat
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Sections

TitleStarting PageNumber of Pages
Table of Contents210
  List of Tables101
  List of Figures111
Introduction121
  Global Markets Direct Report Coverage121
Sickle Cell Disease Overview131
Therapeutics Development142
  Pipeline Products for Sickle Cell Disease Overview141
  Pipeline Products for Sickle Cell Disease Comparative Analysis151
Sickle Cell Disease Therapeutics under Development by Companies164
Sickle Cell Disease Therapeutics under Investigation by Universities/Institutes201
Sickle Cell Disease Pipeline Products Glance214
  Late Stage Products211
  Clinical Stage Products221
  Early Stage Products231
  Unknown Stage Products241
Sickle Cell Disease Products under Development by Companies253
Sickle Cell Disease Products under Investigation by Universities/Institutes281
Sickle Cell Disease Companies Involved in Therapeutics Development2934
  Acceleron Pharma, Inc.291
  Acetylon Pharmaceuticals, Inc.301
  Addex Therapeutics Ltd311
  Advinus Therapeutics Ltd321
  Alnylam Pharmaceuticals, Inc.331
  Angiocrine Bioscience, Inc.341
  Bio Products Laboratory Ltd351
  bluebird bio, Inc.361
  Bristol-Myers Squibb Company371
  Complexa, Inc.381
  CRISPR Therapeutics391
  CSL Limited401
  Editas Medicine, Inc.411
  Emmaus Medical, Inc.421
  Errant Gene Therapeutics, LLC431
  Gamida Cell Ltd.441
  Gilead Sciences, Inc.451
  Global Blood Therapeutics, Inc.461
  Johnson &Johnson471
  La Jolla Pharmaceutical Company481
  Merck &Co., Inc.491
  Modus Therapeutics Holding AB501
  Morphogenesis, Inc.511
  NKT Therapeutics, Inc.521
  Novartis AG531
  Orphagen Pharmaceuticals, Inc.541
  Pfizer Inc.551
  PharmaEssentia Corporation561
  Prolong Pharmaceuticals, LLC571
  Protagonist Therapeutics Inc.581
  ReveraGen BioPharma, Inc.591
  Sancilio &Company, Inc.601
  Sangamo BioSciences, Inc.611
  Selexys Pharmaceuticals Corporation621
Sickle Cell Disease Therapeutics Assessment6312
  Assessment by Monotherapy Products631
  Assessment by Combination Products641
  Assessment by Target653
  Assessment by Mechanism of Action683
  Assessment by Route of Administration712
  Assessment by Molecule Type732
Drug Profiles75108
  (decitabine + tetrahydrouridine) Drug Profile751
  ACY-957 Drug Profile762
  AIC-6020 Drug Profile781
  ALN-TMP Drug Profile792
  ambrisentan Drug Profile812
  apixaban Drug Profile837
  BB-305 Drug Profile907
  benserazide Drug Profile971
  CNTO-530 Drug Profile981
  CordIn Drug Profile991
  CXA-10 Drug Profile1001
  didox Drug Profile1013
  Drugs to Inhibit PRMT5 for Sickle Cell Anemia Drug Profile1041
  DRX-194 Drug Profile1051
  E-CEL-UVEC Drug Profile1061
  EdX-17 Drug Profile1071
  GBT-440 Drug Profile1084
  Gene Therapy for Sickle Cell Anemia Drug Profile1121
  Gene Therapy for Sickle Cell Disease and Thalassemia Drug Profile1131
  Gene Therapy to Activate Gamma Globin for Sickle Cell Disease Drug Profile1141
  glutamine Drug Profile1153
  haptoglobin (human) Drug Profile1181
  haptoglobin + hemopexin Drug Profile1191
  HBI-002 Drug Profile1201
  HBI-137 Drug Profile1211
  hydroxyurea Drug Profile1221
  IMR-687 Drug Profile1231
  LJPC-401 Drug Profile1242
  luspatercept Drug Profile1265
  M-012 Drug Profile1312
  NiCord Drug Profile1333
  NKTT-120 Drug Profile1362
  NM-96 Drug Profile1381
  panobinostat Drug Profile1397
  pentosan polysulfate sodium Drug Profile1461
  PF-04447943 Drug Profile1471
  PNQ-103 Drug Profile1481
  Protein for Sickle Cell Disease Drug Profile1491
  PTG-300 Drug Profile1501
  regadenoson Drug Profile1511
  RN-1 Drug Profile1521
  RNAi Gene Therapy for Sickle Cell Disease and Beta Thalassemia Drug Profile1531
  Sanguinate Drug Profile1542
  SC-411 Drug Profile1561
  SCD-101 Drug Profile1571
  SCPF Drug Profile1581
  SelG-1 Drug Profile1592
  sevuparin sodium Drug Profile1613
  Small Molecule for Beta Thalassemia and Sickle Cell Anemia Drug Profile1641
  Small Molecule for Sickle Cell Disease Drug Profile1651
  Small Molecule to Agonize A2A for Immunology, Hematological and Neurological Disorders Drug Profile1661
  Small Molecules for Sickle Cell Anemia Drug Profile1671
  Small Molecules to Antagonize TNFR1 for Immunology, Gastrointestinal, Neurology and Hematological Disorders Drug Profile1681
  Small Molecules to Inhibit HDAC for Oncology and Sickle Cell Disease Drug Profile1691
  Small Molecules to Inhibit PRMT5 for Haemoglobinopathies and Solid Tumours Drug Profile1701
  sotatercept Drug Profile1715
  Stem Cell Therapy for Beta Thalassemia and Sickle Cell Disease Drug Profile1761
  Stem Cell Therapy for Beta Thalassemia and Sickle Cell Disease Drug Profile1771
  Stem Cell Therapy for Sickle Cell Disease Drug Profile1781
  Stem Cell Therapy to Activate Beta Globin for Sickle Cell Disease Drug Profile1791
  Trichosic Drug Profile1801
  vamorolone Drug Profile1812
Sickle Cell Disease Dormant Projects1833
Sickle Cell Disease Discontinued Products1861
Sickle Cell Disease Product Development Milestones18711
  Featured News &Press Releases1871
    Oct 07, 2016: Global Blood Therapeutics Presents GBT440 Data that Continue to Support Durability, Safety and Mechanism of Action in Sickle Cell Disease1871
    Sep 08, 2016: Emmaus Life Sciences Submits New Drug Application for Sickle Cell Disease Treatment1881
    Sep 07, 2016: La Jolla Pharmaceutical Company Reports Positive Results from Phase 1 Study of LJPC-4011891
    Aug 22, 2016: Emmaus Life Sciences to Seek Marketing Approval for First New Sickle Cell Disease Treatment in Nearly 20 Years; Expects to Submit New Drug Application to FDA in September1891
    Aug 05, 2016: CDSCO requests further data for granting additional indication for Ambrisentan tablet 5mg/10mg1901
    Jul 08, 2016: Global Blood Therapeutics Announces Publication of Preclinical GBT440 Results in British Journal of Haematology that Support Sickle Cell Disease (SCD) Program1901
    Jun 29, 2016: Global Blood Therapeutics Announces Initiation of Phase 2a Study of GBT440 in Adolescents with Sickle Cell Disease1911
    Jun 10, 2016: Global Blood Therapeutics Announces New Clinical Data that Continue to Support Safety and Efficacy Profile of GBT440 as a Potentially Disease-Modifying Therapy for Sickle Cell Disease1912
    Jun 02, 2016: Global Blood Therapeutics to Host Investor Event on Friday, June 10 to Review GBT440 Data in Sickle Cell Disease Being Presented at the European Hematology Associations 21st Congress1931
    May 24, 2016: Hillhurst Biopharmaceuticals Receives SBIR Funding For Development Of HBI-002 For Prevention Of Vaso-Occlusive Crises In Sickle Cell Disease1931
    May 19, 2016: Global Blood Therapeutics Announces Presentation of New GBT440 Data in Sickle Cell Disease at the European Hematology Associations 21st Congress1941
    May 09, 2016: Merganser Biotech Announces Issuance of U.S. Patent 9,315,545 Covering Development Compound M0121941
    May 04, 2016: Acetylon Pharmaceuticals Publishes New Mechanism for the Treatment of Sickle Cell Disease/Beta-Thalassemia with Selective HDAC1/2 Inhibition in PLoS One1951
    Jan 25, 2016: Emmaus Life Sciences Announces Reappointment of Dr. Yutaka Niihara as CEO1961
    Dec 31, 2015: Global Blood Therapeutics Receives FDA Orphan Drug Designation for GBT440 in Sickle Cell Disease1962
Appendix1982
  Methodology1981
  Coverage1981
  Secondary Research1981
  Primary Research1981
  Expert Panel Validation1981
  Contact Us1981
  Disclaimer1991

Table Of Contents

Global Markets Direct - Market Research—Global Markets Direct is a leading provider of global business intelligence and market analysis. It publishes a range of high quality market reports created by its large research and analysis capability and drawing from its extensive unique databases of industry-specific information.

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Cite this Report

  
MLA:
Global Markets Direct - Market Research. "Sickle Cell Disease - Pipeline Review, H2 2016" Oct 29, 2016. Alacra Store. May 04, 2025. <http://www.alacrastore.com/storecontent/Global-Markets-Direct-Market-Research/Sickle-Cell-Disease-Pipeline-Review-H2-2016-2088-16720>
  
APA:
Global Markets Direct - Market Research. (2016). Sickle Cell Disease - Pipeline Review, H2 2016 Oct 29, 2016. New York, NY: Alacra Store. Retrieved May 04, 2025 from <http://www.alacrastore.com/storecontent/Global-Markets-Direct-Market-Research/Sickle-Cell-Disease-Pipeline-Review-H2-2016-2088-16720>
  
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