Sections
Title | Starting Page | Number of Pages |
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Table of Contents | 2 | 4 |
List of Tables | 4 | 1 |
List of Figures | 5 | 1 |
Introduction | 6 | 1 |
Global Markets Direct Report Coverage | 6 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Overview | 7 | 1 |
Therapeutics Development | 8 | 2 |
Pipeline Products for Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Overview | 8 | 1 |
Pipeline Products for Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Comparative Analysis | 9 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Therapeutics under Development by Companies | 10 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Therapeutics under Investigation by Universities/Institutes | 11 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Pipeline Products Glance | 12 | 4 |
Late Stage Products | 12 | 1 |
Clinical Stage Products | 13 | 1 |
Early Stage Products | 14 | 1 |
Unknown Stage Products | 15 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Products under Development by Companies | 16 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Products under Investigation by Universities/Institutes | 17 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Companies Involved in Therapeutics Development | 18 | 7 |
Alkeus Pharmaceuticals, Inc. | 18 | 1 |
Biovista Inc. | 19 | 1 |
GenSight Biologics S.A. | 20 | 1 |
Ixchel Pharma, LLC | 21 | 1 |
Khondrion BV | 22 | 1 |
Spark Therapeutics, Inc. | 23 | 1 |
Stealth BioTherapeutics Inc. | 24 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Therapeutics Assessment | 25 | 9 |
Assessment by Monotherapy Products | 25 | 1 |
Assessment by Target | 26 | 2 |
Assessment by Mechanism of Action | 28 | 2 |
Assessment by Route of Administration | 30 | 2 |
Assessment by Molecule Type | 32 | 2 |
Drug Profiles | 34 | 18 |
BVA-202 Drug Profile | 34 | 1 |
BVA-203 Drug Profile | 35 | 1 |
Drug for Lebers Hereditary Optic Neuropathy Drug Profile | 36 | 1 |
elamipretide Drug Profile | 37 | 6 |
Gene Therapy to Activate ND4 for Leber's Hereditary Optic Neuropathy Drug Profile | 43 | 1 |
GS-010 Drug Profile | 44 | 2 |
GS-011 Drug Profile | 46 | 1 |
IXC-201 Drug Profile | 47 | 1 |
IXC-203 Drug Profile | 48 | 1 |
KH-176 Drug Profile | 49 | 2 |
SPK-LHON Drug Profile | 51 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Dormant Projects | 52 | 1 |
Leber s Hereditary Optic Neuropathy (LHON) (Leber optic atrophy) Product Development Milestones | 53 | 6 |
Featured News &Press Releases | 53 | 1 |
Sep 08, 2016: GenSight Biologics Receives Approval to Include Teenage Patients in RESCUE and REVERSE Phase III Trials with GS010 in Leber s Hereditary Optic Neuropathy | 53 | 1 |
Jun 08, 2016: GenSight Biologics Announces Additional Promising Results of Its Phase I/II Study with GS010 for the Treatment of Leber s Hereditary Optic Neuropathy (LHON) | 54 | 1 |
Jun 01, 2016: Stealth BioTherapeutics Initiates Phase 2 Study of Elamipretide in Leber's Hereditary Optic Neuropathy | 55 | 1 |
Feb 29, 2016: GenSight Biologics Enrolls First Patient in Pivotal Phase III Program of GS010 in Leber s Hereditary Optic Neuropathy | 55 | 2 |
Sep 10, 2015: GenSight Biologics Receives IND Acceptance from FDA to Enter Phase III with GS010 | 57 | 1 |
Dec 15, 2014: New CMO joins Khondrion | 57 | 2 |
Appendix | 59 | 2 |
Methodology | 59 | 1 |
Coverage | 59 | 1 |
Secondary Research | 59 | 1 |
Primary Research | 59 | 1 |
Expert Panel Validation | 59 | 1 |
Contact Us | 59 | 1 |
Disclaimer | 60 | 1 |