Hemophilia A - Pipeline Review, H2 2016 - Global Markets Direct - Market Research

Hemophilia A - Pipeline Review, H2 2016

Hemophilia A - Pipeline Review, H2 2016 - Global Markets Direct - Market Research
Hemophilia A - Pipeline Review, H2 2016
Published Nov 23, 2016
159 pages — Published Nov 23, 2016
Price US$ 2,000.00  |  Buy this Report Now

About This Report

  
Abstract:

Summary

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Hemophilia A Pipeline Review, H2 2016, provides an overview of the Hemophilia A (Hematological Disorders) pipeline landscape.

Hemophilia A is an X-linked, recessive disorder caused by deficiency of functional plasma clotting factor VIII (FVIII), which may be inherited or arise from spontaneous mutation. Depending on the level of FVIII activity, patients with hemophilia may present with easy bruising, inadequate clotting of traumatic injury or in the case of severe hemophilia spontaneous hemorrhage. Symptoms may include bleeding into joints, with associated pain and swelling, blood in the urine or stool, bruising, gastrointestinal tract and urinary tract hemorrhage, nosebleeds, prolonged bleeding from cuts, tooth extraction, and surgery and spontaneous bleeding.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Hemophilia A Pipeline Review, H2 2016, provides comprehensive information on the therapeutics under development for Hemophilia A (Hematological Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Hemophilia A (Hematological Disorders) pipeline guide also reviews of key players involved in therapeutic development for Hemophilia A and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, Preclinical, Discovery and Unknown stages are 5, 8, 4, 4, 21, 2 and 1 respectively. Similarly, the Universities portfolio in Preclinical stages comprises 3 molecules, respectively.Hemophilia A.

Hemophilia A (Hematological Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Directs proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

- The pipeline guide provides a snapshot of the global therapeutic landscape of Hemophilia A (Hematological Disorders).
- The pipeline guide reviews pipeline therapeutics for Hemophilia A (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Hemophilia A (Hematological Disorders) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Hemophilia A (Hematological Disorders) therapeuti

  
Source:
Document ID
GMDHC8692IDB
Industry
Format:
PDF Adobe Acrobat
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Sections

TitleStarting PageNumber of Pages
Table of Contents29
  List of Tables91
  List of Figures101
Introduction111
  Global Markets Direct Report Coverage111
Hemophilia A Overview121
Therapeutics Development132
  Pipeline Products for Hemophilia A Overview131
  Pipeline Products for Hemophilia A Comparative Analysis141
Hemophilia A Therapeutics under Development by Companies152
Hemophilia A Therapeutics under Investigation by Universities/Institutes171
Hemophilia A Pipeline Products Glance184
  Late Stage Products181
  Clinical Stage Products191
  Early Stage Products201
  Unknown Stage Products211
Hemophilia A Products under Development by Companies223
Hemophilia A Products under Investigation by Universities/Institutes251
Hemophilia A Companies Involved in Therapeutics Development2630
  Alnylam Pharmaceuticals Inc261
  Amarna Therapeutics BV271
  Apitope International NV281
  Bayer AG291
  Biogen Inc301
  BioMarin Pharmaceutical Inc311
  Catalyst Biosciences Inc321
  Chugai Pharmaceutical Co Ltd331
  CSL Ltd341
  DBV Technologies SA351
  Dimension Therapeutics Inc361
  Emergent BioSolutions Inc371
  EpiVax Inc381
  Expression Therapeutics LLC391
  Green Cross Corp401
  Idogen AB411
  Lentigen Technology Inc421
  mAbxience SA431
  Novo Nordisk A/S441
  Octapharma AG451
  OPKO Biologics Ltd461
  Pfizer Inc471
  Pharming Group NV481
  rEVO Biologics Inc491
  Sangamo BioSciences Inc501
  Shire Plc511
  SK Chemicals Co Ltd521
  Spark Therapeutics Inc531
  UniQure NV541
  XL-protein GmbH551
Hemophilia A Therapeutics Assessment569
  Assessment by Monotherapy Products561
  Assessment by Target572
  Assessment by Mechanism of Action592
  Assessment by Route of Administration612
  Assessment by Molecule Type632
Drug Profiles6576
  antihemophilic factor Drug Profile654
  antihemophilic factor (human) Drug Profile694
  antihemophilic factor (recombinant) Drug Profile731
  antihemophilic factor (recombinant) Drug Profile741
  antihemophilic factor (recombinant) Drug Profile751
  antihemophilic factor (recombinant) Drug Profile761
  antihemophilic factor (recombinant) Drug Profile771
  antihemophilic factor (recombinant) Drug Profile781
  antihemophilic factor (recombinant) biosimilar Drug Profile791
  antihemophilic factor (recombinant) biosimilar Drug Profile801
  antihemophilic factor (recombinant), pegylated Drug Profile812
  antihemophilic factor (recombinant), single chain Drug Profile833
  ATXF-8117 Drug Profile861
  BAX-888 Drug Profile871
  BAY-1093884 Drug Profile881
  BMN-270 Drug Profile892
  Cell Therapy to Target Coagulation Factor VIII for Hemophilia A Drug Profile911
  coagulation factor VIIa (recombinant) Drug Profile922
  coagulation factor VIII (human) Drug Profile941
  concizumab Drug Profile951
  CSL-689 Drug Profile962
  damoctocog alfa pegol Drug Profile982
  Deimmunized FVIII Drug Profile1001
  DTX-201 Drug Profile1011
  emicizumab Drug Profile1023
  ET-3 Drug Profile1051
  fitusiran Drug Profile1066
  Gene Therapy for Hematological Disorders Drug Profile1121
  Gene Therapy for Hemophilia A Drug Profile1131
  Gene Therapy to Activate Factor VIII for Hemophilia A Drug Profile1141
  IN-3012 Drug Profile1151
  Kovaltry Drug Profile1162
  LG-889 Drug Profile1181
  LR-769 Drug Profile1192
  marzeptacog alfa Drug Profile1212
  MG-1113A Drug Profile1231
  MOD-5014 Drug Profile1243
  PBB-8-IN Drug Profile1271
  PF-06741086 Drug Profile1281
  Recombinant Factor VIII Replacement for Hemophilia A Drug Profile1292
  Recombinant Factor VIII Replacement for Hemophilia A Drug Profile1311
  Recombinant Protein for Hemophilia A Drug Profile1321
  Recombinant Proteins for Hemophilia A Drug Profile1331
  SB-525 Drug Profile1341
  SB-FVIII Drug Profile1352
  SHP-656 Drug Profile1372
  SPK-8011 Drug Profile1391
  SVF-VIIa Drug Profile1401
Hemophilia A Dormant Projects1412
Hemophilia A Discontinued Products1431
Hemophilia A Product Development Milestones14414
  Featured News &Press Releases1441
    Nov 14, 2016: AFSTYLA (rFVIII-SC) - CHMP recommendation1441
    Nov 03, 2016: Genentech to present data on Emicizumab at American Society of Hematology 2016 Annual Meeting1441
    Sep 12, 2016: Idogen reports important breakthrough - positive results from proof-of-concept study in human cells1451
    Aug 26, 2016: Chugai receives Orphan Drug Designation for Emicizumab - Preventing and Reducing the Frequency of Bleeding Episodes in Congenital FVlll Deficiency Patients with Inhibitors1451
    Aug 01, 2016: Shire Announces FDA Approval of adynovate with BAXJECT III Reconstitution System1461
    Jul 27, 2016: CSL Behring Presents Pivotal Efficacy Data for AFSTYLA In Adolescents and Children with Hemophilia A at the World Federation of Hemophilia 2016 World Congress1462
    Jul 27, 2016: Chugai Emicizumab Showed Continued Benefits in Patients with Hemophilia A1481
    Jul 26, 2016: ADYNOVATE Phase 3 Efficacy and Safety Data in Children to be Showcased During International Congress of the World Federation of Hemophilia1491
    Jul 26, 2016: Sangamo BioSciences Announces New Gene Therapy Clinical Development Program for Treatment Of Hemophilia A1501
    Jul 25, 2016: Alnylam Announces New Positive Interim Phase 1 Study Results for Fitusiran, a Once-Monthly, Subcutaneous, Investigational RNAi Therapeutic Targeting Antithrombin for the Treatment of Hemophilia and Rare Bleeding Disorders1513
    Jul 25, 2016: Alnylam to Report New Clinical Results with Fitusiran at the World Federation of Hemophilia 2016 World Congress1541
    Jul 19, 2016: Shire reinforces commitment in Hematology with robust data presented at international congress of the World Federation of Hemophilia1541
    Jul 19, 2016: CSL Behring to Present New Data for AFSTYLA at the World Federation of Hemophilia 2016 World Congress1551
    Jul 18, 2016: Biogen and Sobi to Showcase Data on FVIIIFc-VWF-XTEN at World Federation of Hemophilia 2016 World Congress1561
    Jun 20, 2016: AFSTYLA - CSL Behring Novel Recombinant Factor VIII Single Chain Therapy for Hemophilia A - Now Available in the U.S.1562
Appendix1582
  Methodology1581
  Coverage1581
  Secondary Research1581
  Primary Research1581
  Expert Panel Validation1581
  Contact Us1581
  Disclaimer1591

Table Of Contents

Global Markets Direct - Market Research—Global Markets Direct is a leading provider of global business intelligence and market analysis. It publishes a range of high quality market reports created by its large research and analysis capability and drawing from its extensive unique databases of industry-specific information.

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Cite this Report

  
MLA:
Global Markets Direct - Market Research. "Hemophilia A - Pipeline Review, H2 2016" Nov 23, 2016. Alacra Store. Apr 19, 2024. <http://www.alacrastore.com/storecontent/Global-Markets-Direct-Market-Research/Hemophilia-A-Pipeline-Review-H2-2016-2088-16867>
  
APA:
Global Markets Direct - Market Research. (2016). Hemophilia A - Pipeline Review, H2 2016 Nov 23, 2016. New York, NY: Alacra Store. Retrieved Apr 19, 2024 from <http://www.alacrastore.com/storecontent/Global-Markets-Direct-Market-Research/Hemophilia-A-Pipeline-Review-H2-2016-2088-16867>
  
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