Fabry Disease - Pipeline Review, H2 2016 - Global Markets Direct - Market Research

Fabry Disease - Pipeline Review, H2 2016

Fabry Disease - Pipeline Review, H2 2016 - Global Markets Direct - Market Research
Fabry Disease - Pipeline Review, H2 2016
Published Aug 31, 2016
81 pages — Published Aug 31, 2016
Price US$ 2,000.00  |  Buy this Report Now

About This Report

  
Abstract:

Summary

Global Markets Directs, Fabry Disease - Pipeline Review, H2 2016, provides an overview of the Fabry Disease pipeline landscape.

The report provides comprehensive information on the therapeutics under development for Fabry Disease, complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The report also covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases. Additionally, the report provides an overview of key players involved in therapeutic development for Fabry Disease and features dormant and discontinued projects.

Global Markets Directs report features investigational drugs from across globe covering over 20 therapy areas and nearly 3,000 indications. The report is built using data and information sourced from Global Markets Directs proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Drug profiles featured in the report undergoes periodic review following a stringent set of processes to ensure that all the profiles are updated with the latest set of information. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

The report helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage.

Note*: Certain sections in the report may be removed or altered based on the availability and relevance of data.

Scope

- The report provides a snapshot of the global therapeutic landscape of Fabry Disease
- The report reviews pipeline therapeutics for Fabry Disease by companies and universities/research institutes based on information derived from company and industry-specific sources
- The report covers pipeline products based on various stages of development ranging from pre-registration till discovery and undisclosed stages
- The report features descriptive drug profiles for the pipeline products which includes, product description, descriptive MoA, R&D brief, licensing and collaboration details & other developmental activities
- The report reviews key players involved Fabry Disease therapeutics and enlists all their major and minor projects
- The report assesses Fabry Disease therapeutics based on drug target, mechanism of action (MoA), route of administration (RoA) and molecule type
- The report summarizes all the dormant and discontinued pipeline projects
- The report reviews latest news related to pipeline therapeutics for Fabry Disease

Reasons to buy

- Gain strategically significant competitor information, analysis, and insights to formulate effective R&D strategies
- Identify emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage
- Identify and understand important and diverse types of therapeutics under development for Fabry Disease
- Identify potential new clients or partners in the target demographic
- Develop strategic initiatives by understanding the focus areas of leading companies
- Plan mergers and acquisitions effectively by identifying key players and its most promising pipeline therapeutics
- Devise corrective measures for pipeline projects by understanding Fabry Disease pipeline depth and focus of Indication therapeutics
- Develop and design in

  
Source:
Document ID
GMDHC8415IDB
Industry
Format:
PDF Adobe Acrobat
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Sections

TitleStarting PageNumber of Pages
Table of Contents24
  List of Tables51
  List of Figures51
Introduction61
  Global Markets Direct Report Coverage61
Fabry Disease Overview71
Therapeutics Development81
  Pipeline Products for Fabry Disease Overview81
Fabry Disease Therapeutics under Development by Companies92
Fabry Disease Pipeline Products Glance113
  Late Stage Products111
  Clinical Stage Products121
  Early Stage Products131
Fabry Disease Products under Development by Companies141
Fabry Disease Companies Involved in Therapeutics Development1512
  Actelion Ltd151
  Alexion Pharmaceuticals Inc161
  Amicus Therapeutics, Inc.171
  Genzyme Corporation181
  Greenovation Biotech GmbH191
  ISU ABXIS Co.,Ltd.201
  JCR Pharmaceuticals Co., Ltd.211
  Neuraltus Pharmaceuticals, Inc.221
  Pharming Group N.V.231
  Protalix BioTherapeutics, Inc.241
  Sangamo BioSciences, Inc.251
  Shire Plc261
Fabry Disease Therapeutics Assessment2710
  Assessment by Monotherapy Products271
  Assessment by Combination Products281
  Assessment by Target292
  Assessment by Mechanism of Action312
  Assessment by Route of Administration332
  Assessment by Molecule Type352
Drug Profiles3727
  agalsidase alfa Drug Profile372
  agalsidase alfa Drug Profile391
  agalsidase beta biosimilar Drug Profile401
  AVR-02 Drug Profile411
  Enzyme Replacement Therapy + migalastat hydrochloride Biobetter Drug Profile421
  ibiglustat Drug Profile432
  lucerastat Drug Profile451
  migalastat hydrochloride Drug Profile468
  MOSS-AGAL Drug Profile542
  NP-003 Drug Profile561
  PRX-102 Drug Profile574
  Recombinant Alpha-Galactosidase A Replacement for Fabry Disease Drug Profile611
  Recombinant Enzymes for Pompe, Fabry and Hunter Diseases Drug Profile621
  SBLSD-4 Drug Profile631
Fabry Disease Dormant Projects641
Fabry Disease Discontinued Products651
Fabry Disease Product Development Milestones6614
  Featured News &Press Releases661
    Aug 10, 2016: New England Journal of Medicine Publishes Pivotal Phase 3 FACETS Study of Migalastat for Patients with Fabry Disease661
    Aug 10, 2016: Protalix BioTherapeutics Announces Additional Positive Data from its Phase I/II Clinical Trial for PRX-102 for the Treatment of Fabry Disease671
    Aug 03, 2016: Amicus Therapeutics to Submit Japanese New Drug Application for Migalastat for Fabry Disease in 1H17681
    Aug 02, 2016: Almac Group s Integrated Development to Commercialisation Services Support Amicus Therapeutics First Commercial Orphan Drug Product691
    Jun 06, 2016: Protalix BioTherapeutics Initiates PRX-102 Global Phase III Clinical Trial of Fabry Disease to Support United States and European Filings691
    May 31, 2016: Amicus Therapeutics Announces European Commission Approval for Galafold (Migalastat) in Patients with Fabry Disease in European Union702
    Apr 01, 2016: Amicus Therapeutics Receives Positive CHMP Opinion for Approval of Migalastat in Patients with Fabry Disease in European Union721
    Apr 01, 2016: First oral treatment for Fabry disease recommended for approval in the EU731
    Mar 22, 2016: Amicus Therapeutics Announces Expanded Access Program for Migalastat741
    Mar 03, 2016: Protalix BioTherapeutics Presents Positive Six and Twelve Month Interim Clinical Data on PRX-102 for the Treatment of Fabry Disease at the 12th Annual WORLDSymposium 2016741
    Mar 01, 2016: Amicus Therapeutics Highlights New Phase 3 Fabry Data at WORLDSymposium 2016751
    Feb 22, 2016: Protalix BioTherapeutics to Participate in the SunTrust Robinson Humphrey Orphan Drug Day and the 12th Annual WORLDSymposium 2016761
    Feb 10, 2016: Amicus Therapeutics Announces Presentations on Migalastat at 12th Annual WORLDSymposium 2016761
    Jan 11, 2016: Amicus Therapeutics Provides Update On Migalastat for Fabry Disease771
    Nov 16, 2015: Protalix BioTherapeutics to Conduct Phase III Clinical Trial for PRX-102 for the Treatment of Fabry Disease Following a Successful End-of-Phase II Meeting With FDA782
Appendix802
  Methodology801
  Coverage801
  Secondary Research801
  Primary Research801
  Expert Panel Validation801
  Contact Us801
  Disclaimer811

Table Of Contents

Global Markets Direct - Market Research—Global Markets Direct is a leading provider of global business intelligence and market analysis. It publishes a range of high quality market reports created by its large research and analysis capability and drawing from its extensive unique databases of industry-specific information.

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Cite this Report

  
MLA:
Global Markets Direct - Market Research. "Fabry Disease - Pipeline Review, H2 2016" Aug 31, 2016. Alacra Store. May 14, 2025. <http://www.alacrastore.com/storecontent/Global-Markets-Direct-Market-Research/Fabry-Disease-Pipeline-Review-H2-2016-2088-16484>
  
APA:
Global Markets Direct - Market Research. (2016). Fabry Disease - Pipeline Review, H2 2016 Aug 31, 2016. New York, NY: Alacra Store. Retrieved May 14, 2025 from <http://www.alacrastore.com/storecontent/Global-Markets-Direct-Market-Research/Fabry-Disease-Pipeline-Review-H2-2016-2088-16484>
  
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