Sections
Title | Starting Page | Number of Pages |
---|
Table of Contents | 3 | 7 |
List of Tables | 6 | 2 |
List of Figures | 8 | 2 |
Orphan Disease Therapeutics Market to 2018 - Introduction | 10 | 4 |
Orphan Drug Definitions | 12 | 1 |
The US Orphan Drug Criteria | 12 | 1 |
Europe Orphan Drug Criteria | 12 | 1 |
Japanese Orphan Drug Criteria | 12 | 1 |
Special Cases of Orphan Drug Exclusivity | 12 | 1 |
Comparison of Orphan Drug Designations | 12 | 1 |
GBI Research Report Guidance | 13 | 1 |
Orphan Disease Therapeutics Market to 2018 - Market Characterization | 14 | 4 |
Market Forecasts | 14 | 1 |
Treatment Usage Patterns | 15 | 1 |
Disease Population | 16 | 1 |
Treatment Seeking Population | 16 | 1 |
Diagnosis Population | 17 | 1 |
Prescription Population | 17 | 1 |
Orphan Disease Therapeutics Market to 2010 - Global Fabry s Disease Therapeutics Market | 18 | 8 |
Disease Overview | 18 | 1 |
Market Overview | 18 | 1 |
Revenue by Geographical Segmentation | 19 | 1 |
Annual Cost of Treatment | 20 | 1 |
Treatment Usage Patterns | 21 | 1 |
Disease Population | 22 | 1 |
Treatment Seeking Population | 22 | 1 |
Diagnosis Population | 22 | 1 |
Prescription Population | 22 | 1 |
Marketed Product Analysis | 23 | 1 |
Fabrazyme | 23 | 1 |
Overview | 23 | 1 |
Mechanism of Action | 23 | 1 |
Safety Issues | 23 | 1 |
Efficacy Details | 23 | 1 |
Replagal | 24 | 1 |
Overview | 24 | 1 |
Mechanism of Action | 24 | 1 |
Safety Issues | 24 | 1 |
Efficacy Details | 24 | 1 |
Drug Pipeline Analysis | 25 | 1 |
Pipeline by Phase | 25 | 1 |
Orphan Disease Therapeutics Market to 2018 - Global Pompe Disease Therapeutics Market | 26 | 9 |
Disease Overview | 26 | 1 |
Market Overview | 26 | 2 |
Revenue by Geographical Segmentation | 28 | 1 |
Annual Cost of Treatment | 29 | 1 |
Treatment Usage Patterns | 30 | 1 |
Disease Population | 31 | 1 |
Treatment Seeking Population | 31 | 1 |
Diagnosis Population | 31 | 1 |
Prescription Population | 32 | 1 |
Marketed Product Analysis | 32 | 1 |
Myozyme/Lumizyme | 32 | 1 |
Overview | 32 | 1 |
Mechanism of Action | 32 | 1 |
Safety Issues | 32 | 1 |
Efficacy Details | 33 | 1 |
Drug Pipeline Analysis | 34 | 1 |
Pipeline by Phase | 34 | 1 |
Orphan Disease Therapeutics Market to 2018 - Global Mucopolysaccharidosis VI Disease Therapeutics Market | 35 | 7 |
Disease Overview | 35 | 1 |
Market Overview | 35 | 2 |
Revenue by Geographical Segmentation | 37 | 1 |
Annual Cost of Treatment | 38 | 1 |
Treatment Usage Patterns | 39 | 1 |
Disease Population | 40 | 1 |
Treatment Seeking Population | 40 | 1 |
Diagnosis Population | 40 | 1 |
Prescription Population | 40 | 1 |
Marketed Product Analysis | 41 | 1 |
Naglazyme | 41 | 1 |
Overview | 41 | 1 |
Mechanism of Action | 41 | 1 |
Safety Issues | 41 | 1 |
Efficacy Details | 41 | 1 |
Drug Pipeline Analysis | 41 | 1 |
Orphan Disease Therapeutics Market to 2018 - Global Idiopathic Thrombocytopenic Purpura Disease Therapeutics Market | 42 | 10 |
Disease Overview | 42 | 1 |
Market Overview | 43 | 2 |
Revenue by Geographical Segmentation | 45 | 1 |
Annual Cost of Treatment | 46 | 1 |
Treatment Usage Patterns | 47 | 1 |
Disease Population | 48 | 1 |
Treatment Seeking Population | 48 | 1 |
Diagnosed Population | 48 | 1 |
Prescription Population | 48 | 1 |
Marketed Product Analysis | 49 | 1 |
Nplate (romiplostim) | 49 | 1 |
Promacta/Revolade (eltrombopag) | 49 | 1 |
Rhophylac (Rh0 (D) Immune Globulin (Human)) | 49 | 1 |
Drug Pipeline Analysis | 50 | 1 |
Pipeline by Phase | 51 | 1 |
Orphan Disease Therapeutics Market to 2018 - Global Huntington s Disease Therapeutics Market | 52 | 8 |
Disease Overview | 52 | 1 |
Market Overview | 53 | 1 |
Revenue by Geographical Segmentation | 54 | 1 |
Annual Cost of Treatment | 55 | 1 |
Treatment Usage Patterns | 56 | 1 |
Disease Population | 57 | 1 |
Treatment Seeking Population | 57 | 1 |
Diagnosis Population | 57 | 1 |
Prescription Population | 57 | 1 |
Marketed Product Analysis | 57 | 1 |
Xenazine | 57 | 1 |
Drug Pipeline Analysis | 58 | 1 |
Pipeline by Phase | 58 | 2 |
Orphan Disease Therapeutics Market to 2018 - Global Ovarian Cancer Therapeutics Market | 60 | 14 |
Disease Overview | 60 | 1 |
Market Overview | 60 | 2 |
Revenue by Geographical Segmentation | 62 | 1 |
Average Cost of Therapy | 63 | 1 |
Treatment Usage Patterns | 64 | 1 |
Disease Population | 65 | 1 |
Treatment Seeking Population | 65 | 1 |
Diagnosis Population | 65 | 1 |
Prescription Population | 65 | 1 |
Marketed Product Analysis | 66 | 1 |
Altretamine (hexalen) | 66 | 1 |
Yondelis | 66 | 1 |
Gemzar (gemcitabine) | 66 | 1 |
Drug Pipeline Analysis | 67 | 1 |
Pipeline by Phase | 67 | 7 |
Orphan Disease Therapeutics Market to 2018 - The US Orphan Disease Therapeutics Market | 74 | 4 |
Market Overview | 74 | 1 |
Market Forecasts | 74 | 2 |
Treatment Usage Patterns | 76 | 1 |
Disease Population | 77 | 1 |
Treatment Seeking Population | 77 | 1 |
Diagnosis Population | 77 | 1 |
Prescription Population | 77 | 1 |
Orphan Disease Therapeutics Market to 2018 - Europe Orphan Disease Therapeutics Market | 78 | 4 |
Market Overview | 78 | 1 |
Market Forecasts | 78 | 2 |
Treatment Usage Patterns | 80 | 1 |
Disease Population | 81 | 1 |
Treatment Seeking Population | 81 | 1 |
Diagnosis Population | 81 | 1 |
Prescription Population | 81 | 1 |
Orphan Disease Therapeutics Market to 2018 - Japan Orphan Disease Therapeutics Market | 82 | 4 |
Market Overview | 82 | 1 |
Market Forecasts | 82 | 1 |
Treatment Usage Patterns | 83 | 1 |
Disease Population | 84 | 1 |
Treatment Seeking Population | 84 | 1 |
Diagnosis Population | 85 | 1 |
Prescription Population | 85 | 1 |
Orphan Disease Therapeutics Market to 2018 - Competitive Landscape | 86 | 4 |
Overview | 86 | 1 |
Competitor Profiling | 86 | 1 |
Genzyme/Sanofi | 86 | 1 |
Overview | 86 | 1 |
SWOT Analysis | 87 | 1 |
Shire | 87 | 1 |
Overview | 87 | 1 |
SWOT Analysis | 88 | 1 |
BioMarin | 88 | 1 |
SWOT Analysis | 89 | 1 |
Orphan Disease Therapeutics Market to 2018 - Strategic Consolidations | 90 | 3 |
Mergers and Acquisitions | 90 | 1 |
Sanofi-aventis Completes Acquisition of Genzyme | 90 | 1 |
Deal Summary | 90 | 1 |
Deal Rationale | 90 | 1 |
GlaxoSmithKline Enters into Licensing Agreement with Amicus Therapeutics for Amigal | 91 | 1 |
Amicus Therapeutics Terminates Licensing Agreement with Shire | 91 | 2 |
Orphan Disease Therapeutics Market to 2018 - Orphan Drug Strategies and Future Outlook | 93 | 7 |
Indication Expansion Important for the Orphan Drugs Market | 93 | 1 |
Smaller Companies Find Small Clinical Trials Appealing | 93 | 1 |
Identifying Unique Disease Subsets | 93 | 1 |
Monopoly on a Particular Indication | 93 | 1 |
Genzyme Non-Core Business Out-Licensing Model to Offset Manufacturing Losses | 93 | 1 |
Innovative Risk-sharing Agreements have Emerged as Tools for Providing Market Access | 93 | 1 |
Excessive Pricing of Orphan Drugs by the Pharma Companies Demands Measures for Greater Price Control | 94 | 1 |
Excessive Prices of Orphan Drugs Increase Financial Pressures on Governments | 94 | 1 |
Exploiting Orphan Drug Act; Maximizing Revenue | 94 | 1 |
Ovation s Indocin and Questcor s H.P. Acthar Gel | 95 | 1 |
Pricing an Orphan Drug is Critical to Revenue Generation | 96 | 1 |
Price Control Measures | 96 | 1 |
Global Approach for Orphan Drug Development | 97 | 1 |
Introducing Sales Ceiling and Flexible Market Exclusivity | 97 | 1 |
Price Revisions | 97 | 1 |
GlaxoSmithKline s Retrovir (zidovudine) | 98 | 1 |
Amgen s Epogen (erythropoietin) | 98 | 1 |
Price Control Measures in Orphan Drugs | 99 | 1 |
Orphan Disease Therapeutics Market to 2018 - Appendix | 100 | 7 |
Market Definitions | 100 | 1 |
Abbreviations | 100 | 1 |
Sources | 101 | 1 |
Research Methodology | 102 | 4 |
Coverage | 102 | 1 |
Secondary Research | 102 | 1 |
Primary Research | 102 | 1 |
Epidemiology-Based Forecasting | 103 | 3 |
Contact Us | 106 | 1 |
Disclaimer | 106 | 1 |