Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies - GBI Research Reports

Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies

Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies - GBI Research Reports
Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies
Published Mar 23, 2012
142 pages — Published Mar 23, 2012
Price US$ 3,500.00  |  Buy this Report Now

About This Report

  
Abstract:

Summary

GBI Research has released its latest research, Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies which provides insights into global neurometabolic disorders market and market forecast until 2017. Report is built using data and information sourced from proprietary databases, primary and secondary research and in-house analysis by GBI Researchs team of industry experts. The report provides an in-depth analysis of the Gaucher Disease Type 1, Niemann Pick Type C, Fabry Disease, Pompe Disease and Mucopolysaccharidosis VI Disease. The report examines the treatment usage patterns and also includes insights into the R&D product pipeline and explores the competitive landscape including major players in neurometabolic disorders market. Finally, the report also includes analysis on Mergers and Acquisitions (M&As) and licensing agreements that took place in neurometabolic disorders market.

Scope

- The report analyzes market characterization, pipeline analysis and key M&A trends in the Gaucher Disease Type 1, Niemann Pick Type C, Fabry Disease, Pompe Disease and Mucopolysaccharidosis VI Disease markets in the neurometabolic disorders market.
- Data and analysis on the contraceptives market in the leading geographies of the world the US, the UK, Germany, France, Italy, Spain, and Japan.
- Annualized market data for the Gaucher Disease Type 1, Niemann Pick Type C, Fabry Disease, Pompe Disease and Mucopolysaccharidosis VI Disease in the neurometabolic disorders market from 2002 to 2010, with forecasts to 2017.
- Market data on the therapeutic landscape which covers market revenues, treatment usage patterns and annual cost of therapy.
- Key drivers and restraints that have had a significant impact on the market
- The competitive landscape of the neurometabolic disorders market.
- Key M&A activities and Licensing Agreements that took place from 2005 to 2011 in the contraceptives market.

Reasons to buy

- Align your product portfolio to the markets with high growth potential.
- Develop market-entry and market expansion strategies by identifying the potential region and therapeutic segments poised for strong growth.
- Device a more tailored country strategy through the understanding of key drivers and barriers of the neurometabolic disorders market.
- Develop key strategic initiatives by understanding the key focus areas of leading companies.
- Accelerate and strengthen your market position by identifying key companies for mergers, acquisitions and strategic partnerships.

  
Source:
Document ID
GBIHC145MR
Industry
Format:
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Sections

TitleStarting PageNumber of Pages
Table of Contents48
  List of Tables73
  List of Figures102
Neurometabolic Disorders Market to 2017 - Introduction122
  GBI Research Report Guidance131
Neurometabolic Disorders Market to 2017 - Global Market Overview146
  Introduction141
  Market Revenue142
  Annual Cost of Therapy161
    Treatment Usage Pattern171
      Diseased Population181
      Treatment Seeking Population181
      Diagnosed Population181
      Prescription Population191
Neurometabolic Disorders Market to 2017 - Geographical Landscape2015
  The US211
    Revenue212
    Annual Cost of Therapy231
    Treatment Usage Pattern241
      Diseased Population251
      Treatment Seeking Population251
      Diagnosed Population251
      Prescription Population261
  Top Five Countries of Europe261
    Revenue262
    Annual Cost of Therapy281
    Treatment Usage Pattern291
      Diseased Population301
      Treatment Seeking Population301
      Diagnosed Population301
      Prescription Population301
  Japan311
    Revenue311
    Annual Cost of Therapy321
    Treatment Usage Pattern331
      Diseased Population341
      Treatment Seeking Population341
      Diagnosed Population341
      Prescription Population341
Neurometabolic Disorders Market to 2017 - Therapeutic Landscape3547
  Neurometabolic Disorders Market to 2017 - Gaucher s Disease351
    Introduction351
    Revenue362
    Revenue by Geography382
    Annual Cost of Therapy401
    Treatment Usage Pattern411
      Diseased Population411
      Treatment Seeking Population421
      Diagnosed Population421
      Prescription Population421
    Treatment Algorithm431
    Gaucher s Type 1 Disease Therapeutics Market Drivers441
      Promising Pipeline Molecules in Late stage of Development441
      Increase in Awareness Levels among Gaucher s Patients441
    Gaucher s Type 1 Disease Therapeutics Market Restraints451
      Low Diagnosis Rate451
      High Treatment Cost451
  Neurometabolic Disorders Market to 2017 - Niemann-Pick Type C Disease451
    Introduction452
    Revenue471
    Revenue by Geography482
    Annual Cost of Therapy501
    Treatment Usage Pattern511
      Diseased Population511
      Treatment Seeking Population521
      Diagnosed Population521
      Prescription Population521
    Treatment Algorithm531
    Niemann-Pick Type C Market Drivers541
      Increase in Disease Awareness541
      Increase in Drug Uptake in Europe and Other Countries551
    Niemann-Pick Type C Market Restraints551
      Lack of Approval and Reimbursement of Zavesca in the US and Japan551
      Misdiagnosis551
  Neurometabolic Disorders Market to 2017 - Pompe Disease561
    Introduction561
    Revenue562
    Revenue by Geography582
    Annual Cost of Therapy601
    Treatment Usage Pattern611
      Diseased Population621
      Treatment Seeking Population621
      Diagnosed Population621
      Prescription Population631
    Treatment Algorithm631
    Pompe Disease Therapeutics Market Drivers641
      Approval of Lumizyme and Strong Growth in Sales of Marketed Drugs641
      Increase in Disease Awareness and Increased Support for Medical Research641
    Pompe Disease Therapeutics Market Restraints651
      Poor Diagnosis and Treatment Seeking Rate651
      High Cost of Therapy651
  Neurometabolic Disorders Market to 2017 - Fabry Disease651
    Introduction651
    Revenue652
    Revenue by Geography672
    Annual Cost of Therapy691
    Treatment Usage Pattern701
      Diseased Population711
      Treatment Seeking Population711
      Diagnosed Population711
      Prescription Population711
    Fabry Disease Therapeutics Market Drivers721
      Promising Late Stage Pipeline Molecules (Pharmacological Chaperones) for the Treatment of Fabry Disease721
      Increase in Awareness Levels of Disease Progression and Etiology721
    Fabry Disease Therapeutics Market Restraints731
      Misdiagnosis of Fabry Disease731
      High Annual Cost of the Treatment731
  Neurometabolic Disorders Market to 2017 - Mucopolysaccharidosis VI731
    Introduction731
    Revenue741
    Revenue by Geography751
    Annual Cost of Therapy761
    Treatment Usage Pattern771
      Diseased Population781
      Treatment Seeking Population781
      Diagnosed Population781
      Prescription Population781
    Treatment Algorithm791
    Mucopolysaccharidosis VI Therapeutics Market Drivers801
      Strong Performance by Existing Branded Drugs801
      Increase in Disease Awareness801
    Mucopolysaccharidosis VI Therapeutics Market Restraints811
      Poor Diagnosis Rate811
Neurometabolic Disorders Market to 2017 - Major Marketed Products8210
  Gaucher s Disease821
    Cerezyme821
      Overview821
      Mechanism of Action821
      Efficacy Details821
      Safety Issues831
    VPRIV831
      Overview831
      Mechanism of Action841
      Efficacy Details841
      Safety Issues841
  Gaucher s Disease and Niemann-Pick Type C851
    Zavesca851
      Overview851
      Mechanism of Action851
      Efficacy Details851
      Safety Issues861
  Pompe Disease861
    Myozyme/Lumizyme861
      Overview861
      Mechanism of Action861
      Efficacy Details871
      Safety Issues881
  Fabry Disease881
    Fabrazyme881
      Overview881
      Mechanism of Action881
      Efficacy Details881
      Safety Issues891
    Replagal891
      Overview891
      Mechanism of Action891
      Efficacy Details891
      Safety Issues901
  Mucopolysaccharidosis VI911
    Naglazyme911
      Overview911
      Mechanism of Action911
      Efficacy Details911
      Safety Issues911
Neurometabolic Disorders Market to 2017 - Product Pipeline Analysis9211
  Gaucher s Disease - Research and Development Pipeline941
    Overview941
    Pipeline by Phase941
  Niemann-Pick Type C: Research and Development Pipeline951
    Overview951
    Pipeline by Phase951
  Pompe Disease: Research and Development Pipeline961
    Overview961
    Pipeline by Phase961
  Fabry Disease: Research and Development Pipeline971
    Overview971
    Pipeline by Phase971
  Most Promising Molecules981
    Uplyso981
      Overview981
      Mechanism of Action981
      Research and Development Brief981
      Discovery/Preclinical Trial Details991
    Genz-112638991
      Overview991
      Mechanism of Action991
      Phase III Trials1001
      Phase II Trials1001
    Amigal1011
      Overview1011
      Mechanism of Action1011
      Phase III Trials1011
      Phase II Trials1011
      Phase I Trials1021
      Other Developmental Activities1021
Neurometabolic Disorders Market to 2017- Competitive Landscape10325
  Overview1032
  Company Profiles1051
    Genzyme Corporation1051
      Overview1051
      SWOT Analysis1051
      Deals1067
    Shire1131
      Overview1131
      SWOT Analysis1131
      Deals1146
    BioMarin Pharmaceutical Inc.1201
      Overview1201
      SWOT Analysis1211
      Deals1222
    Actelion1241
      Overview1241
      SWOT Analysis1251
      Deals1262
Neurometabolic Disorders Market to 2017 - Strategic Consolidations1287
  Overview1281
    Sanofi S.A. Completes Acquisition of Genzyme1291
      Deal Summary1291
      Deal Rationale1291
    Pfizer Enters into a Licensing Agreement with Protalix Biotherapeutics1301
    GlaxoSmithKline Enters into Licensing Agreement with Amicus Therapeutics for Amigal1301
    Amicus Therapeutics Terminates Licensing Agreement with Shire1311
  Deals by Geography1311
  Deals by Licensing Type1321
  Deals by Value1331
  Deals by Phase1341
    NDA Filed1341
      Taliglucerase alpha1341
    Phase III1341
      Amigal1341
Neurometabolic Disorders Market to 2017 - Appendix1358
  Market Definitions1351
  Abbreviations1351
  Research Methodology1362
    Coverage1361
    Secondary Research1371
    Primary Research1371
  Therapeutic Landscape1383
    Epidemiology-based Forecasting1382
    Market Size by Geography1401
  Geographical Landscape1411
  Pipeline Analysis1411
  Competitive Landscape1411
    Expert Panel Validation1411
  Contact Us1411
  Disclaimer1411
  Sources1421

Table Of Contents

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Cite this Report

  
MLA:
GBI Research Reports. "Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies" Mar 23, 2012. Alacra Store. May 11, 2025. <http://www.alacrastore.com/storecontent/GBI-Research-Reports/Neurometabolic-Disorders-Market-to-2017-Novel-Therapies-for-Rare-Diseases-such-as-Gauchers-and-Niemann-Pick-Poised-to-Supersede-Existing-Therapies-2115-380>
  
APA:
GBI Research Reports. (2012). Neurometabolic Disorders Market to 2017 - Novel Therapies for Rare Diseases such as Gauchers and Niemann-Pick Poised to Supersede Existing Therapies Mar 23, 2012. New York, NY: Alacra Store. Retrieved May 11, 2025 from <http://www.alacrastore.com/storecontent/GBI-Research-Reports/Neurometabolic-Disorders-Market-to-2017-Novel-Therapies-for-Rare-Diseases-such-as-Gauchers-and-Niemann-Pick-Poised-to-Supersede-Existing-Therapies-2115-380>
  
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